正在加载图片...
and scalable two-step ion-exchange chromatography pro- tors by ion-exchange chromatography J. Hum Gene Ther cess for the purification of recombinant adeno-associated Methods,2012,23(1):56 irus serotypes-2 and-5[J]. Mol Ther, 2002. 6(5): 678 [33 Ye G, Scotti MM, Thomas DL, et al. Herpes simplex vi- [19] Potter M, Lins B, Mietzsch M, et al. A simplified purifi- us clearance during purification of a recombinant adeno- cation protocol for recombinant adeno-associated virus associated virus serotype I vectorJ]. Hum Gene Thei ectorsJ]. Mol Ther Methods Clin Dev, 2014, de Clin dey,2014,doi:10.1089/humc.2014.060. 10.1038/mtm.2014.34 34 Murray S, Nilsson CL, Hare JT, et al. Characterization of [20 Cronin T, Vandenberghe LH, Hantz P, et al. Efficien transduction and optogenetic stimulation of retinal bipolar type 2 by high-resolution mass spectrometry[].J Virol. ells by a synthetic adeno-associated virus capsid and pro- 2006,80(12):6171 moter[J]. EMBO Mol Med, 2014, 6(9): 1 175 35 Wolff MW, Reichl U. Downstream processing of cell cul [21 Harbison CE, Weichert Ws, Gurda BL, et al. Examini ure-derived virus particles[]. Expert Rev vaccines the cross-reactivity and neutralization mechanisms of a 2011,10(10):1451 panel of mAbs against adeno-associated virus serotypes 1 [36 Doria M, Ferrara A, Auricchio A AAV2/8 vectors puri and 5[J].J Gen Virol, 2012, 93(Pt 2): 347 fied from culture medium with a simple and rapid proto Smith RH, Levy JR, Kotin RM. A simplified baculovirus- col transduce murine liver, muscle, andretina efficiently AAV expression vector system coupled with one-step af- []. Hum Gene Ther Methods, 2013, 24(6): 392 finity purification yields high- -titer TAav stocks from in-[37]P·MQ·谢尔登,P·S·加尼翁,G·尼科尔斯,等用于纯 sect cells[J]. Mol Ther, 2009, 17(11): 1 888 化重组AAV载体的改进方法:中国,2010800270123 [23] Naumer M, Sonntag F, Schmidt K, et al. Properties of [P]2010-06-16 the adeno-associated virus assembly-activating protein[J]. [38 Ayuso E, Mingozzi F, Bosch F Production, purification , Virol,2012,86(23):13038 and characterization of adeno-associated vectors]. Curr [24 Arnold GS, Sasser AK. Stachler MD, et al. Metabolic bio Gene Ther,2010,10(6):423 tinylation provides a unique platform for the purification [39] Zhou J, Yang X, Wright JF, et al. PEG-nmodulated column and targeting of multiple AAv vector serotypes[p]. Mol chromatography for purification of recombinant adeno-as- Ther,2006,14(1):9 sociated virus serotype 9p.J/ Methods, 2011, 173 [25 Koerber JT. Jang JH, Yu JH, et al. Engineering adeno-as- sociated virus for one-step purification via immobilized [40 Debelak D, Fisher J, luliano S, et al. Cation-exchange metal affinity chromatography ] Hum Gene Ther. 2007 high-performance liquid chromatography of recombinant 18(4):367 adeno-associated virus type 2[].J Chromatogr B Biomed 26 Shen S, Troupes AN, Pulicherla N, et al. Multiple role Sci Appl,2000,740(2):19 sialylated glycans in determining the cardiopulmonary t (41 Okada T, Nonaka-Sarukawa M, Uchibori R, et al. Scal pism of adeno-associated virus 4[J]. J Virol, 2013, 87(24) able purification of adeno-associated virus serotype 13206 (AAV1) and AAV8 vectors, using dual ion-exchange ad- 27 Stachler MD, Bartlett Js. Mosaic vectors comprised of sorptive membranes[J]. Hum Gene Ther, 2009, 20(9) modified AAVI capsid proteins for efficient vector puri 1013. cation and targeting to vascular endothelial cells]. Gene [42 Duffy AM, O Doherty AM. O Brien T, et al. Purification er,2006,13(11):926 of adenovirus and adeno-associated virus: comparison of [28 Munch RC, Muth A, Muik A, et al. Off-target-free gene novel membrane-based technology to conventional tech- delivery by affinity-purified receptor-targeted viral vectors niques[J]. Gene Ther, 2005, 12(1): 62. U]. Nat Commun, 2015, doi: 10.1038/ncomms7246 43 Orr V. Zhong L, Moo- Young M, et al. Recent advances 29 Wright JF. AAV empty capsids: for better or for worse? in bioprocessing application of membrane chromatography 门] Mol wher,2014,22(1):1 []. Biotechnol Adv, 2013, 31(4): 450 30] Venkatakrishnan B. Yarbrough J. Domsic J, et al. Struc- [44] Burova E, loffe E. Chromatographic purification of re- ture and dynamics of adeno-associated virus serotype combinant adenoviral and adeno-associated viral vecto VPl-unique N-terminal domain and its role in capsid traf- methods and implications[J]. Gene Ther. 2005, 12(1):5 ficking[ virol,2013,87(9):4974 [45 Dreesen IAJ, Luchinger NA, Stark WJ, et al. Tricalcium [31 Qu W. Wang M, Wu Y, et al. Calcium-ion-modulated ce- phosphate nanoparticles enable rapid purification, in- ramic hydroxyapatite resin for the scalable purification of crease transduction kinetics, and modify the tropism of recombinant adeno-associated virus serotype 9p].J Chro- mammalian viruses[J]. Biotechnol Bioeng, 2009, 102(4) matogr B Analyt Technol Biomed Life Sci, 2015, do 10.1016/ chroma.2015.03.003 146 Ariza L, Gimenez-Llort L, Cubizolle A, et al. Central [32] Lock M, Alvira MR, Wilson JM. Analysis of particle con- nervous system delivery of helper-dependent canine ade tent of recombinant adeno-associated virus serotype 8 vec novirus corrects neuropathology and behavior in muco- 中国药房2015年第26卷第34期 China Pharmacy 2015 Vol 26 No 34 .4883中国药房 2015年第26卷第34期 China Pharmacy 2015 Vol. 26 No. 34 and scalable two-step ion-exchange chromatography pro￾cess for the purification of recombinant adeno-associated virus serotypes-2 and -5[J]. Mol Ther,2002,6(5):678. [19] Potter M,Lins B,Mietzsch M,et al. A simplified purifi￾cation protocol for recombinant adeno-associated virus vectors[J]. Mol Ther Methods Clin Dev,2014,doi: 10.1038/mtm.2014.34. [20] Cronin T,Vandenberghe LH,Hantz P,et al. Efficient transduction and optogenetic stimulation of retinal bipolar cells by a synthetic adeno-associated virus capsid and pro￾moter[J]. EMBO Mol Med,2014,6(9):1 175. [21] Harbison CE,Weichert WS,Gurda BL,et al. Examining the cross-reactivity and neutralization mechanisms of a panel of mAbs against adeno-associated virus serotypes 1 and 5[J]. J Gen Virol,2012,93(Pt 2):347. [22] Smith RH,Levy JR,Kotin RM. A simplified baculovirus￾AAV expression vector system coupled with one-step af￾finity purification yields high-titer rAAV stocks from in￾sect cells[J]. Mol Ther,2009,17(11):1 888. [23] Naumer M,Sonntag F,Schmidt K,et al. Properties of the adeno-associated virus assembly-activating protein[J]. J Virol,2012,86(23):13 038. [24] Arnold GS,Sasser AK,Stachler MD,et al. Metabolic bio￾tinylation provides a unique platform for the purification and targeting of multiple AAV vector serotypes[J]. Mol Ther,2006,14(1):97. [25] Koerber JT,Jang JH,Yu JH,et al. Engineering adeno-as￾sociated virus for one-step purification via immobilized metal affinity chromatography[J]. Hum Gene Ther,2007, 18(4):367. [26] Shen S,Troupes AN,Pulicherla N,et al. Multiple roles for sialylated glycans in determining the cardiopulmonary tro￾pism of adeno-associated virus 4[J]. J Virol,2013,87(24): 13 206. [27] Stachler MD,Bartlett JS. Mosaic vectors comprised of modified AAV1 capsid proteins for efficient vector purifi￾cation and targeting to vascular endothelial cells[J]. Gene Ther,2006,13(11):926. [28] Münch RC,Muth A,Muik A,et al. Off-target-free gene delivery by affinity-purified receptor-targeted viral vectors [J]. Nat Commun,2015,doi:10.1038/ncomms7246. [29] Wright JF. AAV empty capsids:for better or for worse? [J]. Mol Ther,2014,22(1):1. [30] Venkatakrishnan B,Yarbrough J,Domsic J,et al. Struc￾ture and dynamics of adeno-associated virus serotype 1 VP1-unique N-terminal domain and its role in capsid traf￾ficking[J]. J Virol,2013,87(9):4 974. [31] Qu W,Wang M,Wu Y,et al. Calcium-ion-modulated ce￾ramic hydroxyapatite resin for the scalable purification of recombinant adeno-associated virus serotype 9[J]. J Chro￾matogr B Analyt Technol Biomed Life Sci,2015,doi: 10.1016/j.jchromb.2015.03.003. [32] Lock M,Alvira MR,Wilson JM. Analysis of particle con￾tent of recombinant adeno-associated virus serotype 8 vec￾tors by ion-exchange chromatography[J]. Hum Gene Ther Methods,2012,23(1):56. [33] Ye GJ,Scotti MM,Thomas DL,et al. Herpes simplex vi￾rus clearance during purification of a recombinant adeno￾associated virus serotype 1 vector[J]. Hum Gene Ther Clin Dev,2014,doi:10.1089/humc.2014.060. [34] Murray S,Nilsson CL,Hare JT,et al. Characterization of the capsid protein glycosylation of adeno-associated virus type 2 by high-resolution mass spectrometry[J]. J Virol, 2006,80(12):6 171. [35] Wolff MW,Reichl U. Downstream processing of cell cul￾ture-derived virus particles[J]. Expert Rev Vaccines, 2011,10(10):1 451. [36] Doria M,Ferrara A,Auricchio A. AAV2/8 vectors puri￾fied from culture medium with a simple and rapid proto￾col transduce murine liver,muscle,andretina efficiently [J]. Hum Gene Ther Methods,2013,24(6):392. [37] P·M·Q·谢尔登,P·S·加尼翁,G·尼科尔斯,等.用于纯 化重组 AAV 载体的改进方法:中国,2010800270123 [P]. 2010-06-16. [38] Ayuso E,Mingozzi F,Bosch F. Production,purification and characterization of adeno-associated vectors[J]. Curr Gene Ther,2010,10(6):423. [39] Zhou J,Yang X,Wright JF,et al. PEG-modulated column chromatography for purification of recombinant adeno-as￾sociated virus serotype 9[J]. J Virol Methods,2011,173 (1):99. [40] Debelak D,Fisher J,Iuliano S,et al. Cation-exchange high-performance liquid chromatography of recombinant adeno-associated virus type 2[J]. J Chromatogr B Biomed Sci Appl,2000,740(2):195. [41] Okada T,Nonaka-Sarukawa M,Uchibori R,et al. Scal￾able purification of adeno-associated virus serotype 1 (AAV1)and AAV8 vectors,using dual ion-exchange ad￾sorptive membranes[J]. Hum Gene Ther,2009,20(9): 1 013. [42] Duffy AM,O’Doherty AM,O’Brien T,et al. Purification of adenovirus and adeno-associated virus:comparison of novel membrane-based technology to conventional tech￾niques[J]. Gene Ther,2005,12(1):62. [43] Orr V,Zhong L,Moo-Young M,et al. Recent advances in bioprocessing application of membrane chromatography [J]. Biotechnol Adv,2013,31(4):450. [44] Burova E,Ioffe E. Chromatographic purification of re￾combinant adenoviral and adeno-associated viral vectors: methods and implications[J]. Gene Ther,2005,12(1):5. [45] Dreesen IAJ,Lüchinger NA,Stark WJ,et al. Tricalcium phosphate nanoparticles enable rapid purification, in￾crease transduction kinetics,and modify the tropism of mammalian viruses[J]. Biotechnol Bioeng,2009,102(4): 1 197. [46] Ariza L,Giménez-Llort L,Cubizolle A,et al. Central nervous system delivery of helper-dependent canine ade￾novirus corrects neuropathology and behavior in muco- ·4883·
<<向上翻页向下翻页>>
©2008-现在 cucdc.com 高等教育资讯网 版权所有